盐酸美格鲁特
Miglustat Hydrochloride (N-Butyldeoxynojirimycin Hydrochloride; NB-DNJ hydrochloride; OGT918 hydrochloride)
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基本信息
中文名称盐酸美格鲁特
英文名称 Miglustat Hydrochloride (N-Butyldeoxynojirimycin Hydrochloride; NB-DNJ hydrochloride; OGT918 hydrochloride)
CAS号210110-90-0
分子式C10H21NO4.HCl
分子量255.74
外观 White to light brown
储存条件 Dry, dark and at 0 - 4℃ for short term (days to weeks) or -20℃ for long term (months to years).
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产品详情

 Miglustat, also known as OGT 918 and NB-DNJ, is a drug developed by Actelion and is used primarily to treat Type I Gaucher disease (GD1). Miglustat inhibits glucosylceramide synthase, an essential enzyme for the synthesis of most glycosphingolipids (it forms glucosylceramide and accumulates within the macrophages).

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